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Hyperammonemia in Inherited Metabolic Diseases

Correction of methylmalonic aciduria in vivo using a codon-optimized lentiviral vector
Toxicol in Vitro 27(6):18301837

Vehculo c.s.p

doi: 10.1016/j.rbmo.2023.103770 [DOI] [PubMed] [Google Scholar] 34